Hemophilia Therapeutics Pipeline to Witness Major Collaborations in The Future

  • Published: June 2017

According to a new research report “Hemophilia Therapeutics Pipeline Analysis, 2017 - Clinical Trials & Results, Patent, Designation, Collaboration, and Other Developments” published by P&S Intelligence, Hemophilia currently exhibits a strong pipeline with 53 drug candidates.

Explore Report Description at:

Hemophilia pipeline in 2017

The study analysed that the hemophilia pipeline comprises of 53 drug candidates in different stages of development.

Insights on pipeline segments

The pipeline analysis based on route of administration of active drug candidates showed, that around most of the hemophilia drug candidates are being developed to be administered by intravenous route.

Increasing collaboration between educational institutes, medical associations and pharma companies

Most of the pharma and biotech companies are developing the therapeutics for hemophilia in collaboration with educational institutes. In September 2016, Roche in collaboration with Chugai Pharmaceutical Co. Ltd. initiated a Phase III trial to evaluate the safety, pharmacokinetics and efficacy of prophylactic subcutaneous emicizumab in patients (aged 12 years) suffering from hemophilia A without factor VIII inhibitors.

Various drug candidates received, Fast Track or Breakthrough Designation for the treatment of hemophilia

Many drug candidates received USFDA designations namely Orphan, Fast Track or Breakthrough designations in their clinical stages for the treatment of hemophilia. In August 2016, Orphan Drug Designation was granted to Phase III drug candidate of Chugai Pharmaceuticals, by Ministry of Health, Labour and Welfare, Japan.

Some of the key players developing drugs for the treatment of hemophilia include Sangamo BioSciences, Inc., Caisson Biotech, Inc., XL-protein GmbH, and others.

Hemophilia Pipeline Analysis

  • By Phase
  • By Route of Administration
  • By Molecule Type
  • By Company